winning duchenne

Our nonprofit organization was established to give equal opportunity to life for all Duchenne children who have rare mutations, with the understanding of the daily struggle every family with a child with Duchenne is facing, and all the more so with rare mutations. Support the research for the development of specific mutation-adapted drugs that will delay the development of the disease, focusing on rare mutations. Support the research for the development of customized drugs for the cure of the disease using genetic modification technology (CRISPR), which enables the ‘cutting’ of the damaged DNA and its replacement with a normal section of DNA. Encouraging projects that work for the benefit of patients, and support the medical community that treats Duchenne disease worldwide. Raising awareness in Israel and around the world of the Duchenne disease. Development of custom drugs for Duchenne children who have rare mutations. The development of drugs for orphan diseases is a very expensive process, estimated at millions of shekels, all the more so when it comes to rare mutations and in light of the small number of patients, the drug companies have no economic viability to develop treatments and drugs.